2024Molecular therapy. Methods & clinical development32 (4) : 101348
What's in a word? Defining "gene therapy medicines"
von Fritschen M, Janosz E, Blume C, Jägle U, Keating K, Schneider C
von Fritschen M, Janosz E, Blume C, Jägle U, Keating K, Schneider C