Human Lentiviral Gene Therapy Restores the Cellular Phenotype of Autosomal Recessive Complete IFN-γR1 Deficiency
Hahn K, Pollmann L, Nowak J, Nguyen A, Haake K, Neehus A, Waqas S, Pessler F, Baumann U, Hetzel M, Casanova J, Schulz A, Bustamante J, Ackermann M, Lachmann N